SAYS - 02 Jun 2023
"And it turns out that I am also a carrier. So the risk of thalassemia major is there. And we can't afford the uncertainties," she wrote.
European Medicines Agency | - 15 Dec 2023
First gene editing therapy to treat beta thalassemia and severe sickle cell disease | European Medicines Agency ...
Nature.com - 21 Aug 2023
Long-term clinical efficacy and safety of thalidomide in patients with transfusion-dependent β-thalassemia: results from ... ...