prader–willi syndrome

Community races together for Prader-Willi Syndrome Research » Giving » UF Health » University of Florida

UF Health - 12 Mar 2024
Community races together for Prader-Willi Syndrome Research » Giving » UF Health » University of Florida ...

Similar metabolic pathways are affected in both Congenital Myasthenic Syndrome-22 and Prader-Willi Syndrome

ScienceDirect.com - 16 Apr 2024
Similar metabolic pathways are affected in both Congenital Myasthenic Syndrome-22 and Prader-Willi Syndrome ...

Persistent shortage of growth hormone frustrates parents and clinicians |

WBUR News - 17 Apr 2024
Persistent shortage of growth hormone frustrates parents and clinicians | ...

Analysis of Hyperphagia Questionnaire for Clinical Trials (HQ-CT) scores in typically developing individuals and those ...

Nature.com - 23 Nov 2023
Analysis of Hyperphagia Questionnaire for Clinical Trials (HQ-CT) scores in typically developing individuals and those ... ...

Woman with Prader-Willi syndrome celebrates graduation with family

Bay News 9 - 12 Dec 2023
Woman with Prader-Willi syndrome celebrates graduation with family ...

Harmony wins orphan drug tag for pitolisant to treat Prader-Willi syndrome

Pharmaceutical Technology - 22 Feb 2024
Harmony wins orphan drug tag for pitolisant to treat Prader-Willi syndrome ...

Prader-Willi Syndrome Market is Likely to Increase at a Steady Growth Rate by 2032, Estimates DelveInsight | Leading ...

PR Newswire - 13 Nov 2023
Prader-Willi Syndrome Market is Likely to Increase at a Steady Growth Rate by 2032, Estimates DelveInsight | Leading ... ...

Study: Some symptoms of PWS are more common with deletion mutations

Prader-Willi Syndrome News - 02 Feb 2024
Study: Some symptoms of PWS are more common with deletion mutations ...

TNX-2900 to treat Prader-Willi syndrome granted Rare Pediatric Disease designation

Contemporary Pediatrics - 25 Mar 2024
TNX-2900 to treat Prader-Willi syndrome granted Rare Pediatric Disease designation ...

Soleno (SLNO) Soars as Prader-Willi Syndrome Study Meets Goal

Yahoo Finance - 27 Sep 2023
Soleno (SLNO) Soars as Prader-Willi Syndrome Study Meets Goal ...

Harmony Biosciences Gets FDA Orphan Designation for Pitolisant in Prader-Willi Syndrome

MarketWatch - 20 Feb 2024
Harmony Biosciences Gets FDA Orphan Designation for Pitolisant in Prader-Willi Syndrome ...

Defects in early synaptic formation and neuronal function in Prader-Willi syndrome | Scientific Reports

Nature.com - 25 Jul 2023
Defects in early synaptic formation and neuronal function in Prader-Willi syndrome | Scientific Reports ...

HARMONY BIOSCIENCES RECEIVES U.S. FOOD AND DRUG ADMINISTRATION ORPHAN DRUG DESIGNATION ...

PR Newswire - 20 Feb 2024
HARMONY BIOSCIENCES RECEIVES U.S. FOOD AND DRUG ADMINISTRATION ORPHAN DRUG DESIGNATION ... ...

Tool capturing hyperphagia in Prader-Willi trials of use in real life

Prader-Willi Syndrome News - 04 Jan 2024
Tool capturing hyperphagia in Prader-Willi trials of use in real life ...

HARMONY BIOSCIENCES INITIATES GLOBAL PHASE 3 REGISTRATIONAL TRIAL (TEMPO STUDY) OF PITOLISANT ...

PR Newswire - 03 Apr 2024
HARMONY BIOSCIENCES INITIATES GLOBAL PHASE 3 REGISTRATIONAL TRIAL (TEMPO STUDY) OF PITOLISANT ... ...

Differential DNA methylation in iPSC-derived dopaminergic neurons: a step forward on the role of SNORD116 ...

Nature.com - 02 Apr 2024
Differential DNA methylation in iPSC-derived dopaminergic neurons: a step forward on the role of SNORD116 ... ...

HARMONY BIOSCIENCES PRESENTS NEW SECONDARY OUTCOME DATA FROM PHASE 2 SIGNAL DETECTION ...

PR Newswire - 05 Oct 2023
HARMONY BIOSCIENCES PRESENTS NEW SECONDARY OUTCOME DATA FROM PHASE 2 SIGNAL DETECTION ... ...

Patients at the Heart win will help fund PWSA's sleep disorder effort

Prader-Willi Syndrome News - 02 Nov 2023
Patients at the Heart win will help fund PWSA's sleep disorder effort ...

Pitolisant Shows Promise for Prader-Willi Syndrome Symptoms

Sleep Review - 06 Oct 2023
Pitolisant Shows Promise for Prader-Willi Syndrome Symptoms ...