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Leben mit Rett-Syndrom: Plötzlich kamen keine Worte mehr - FAZ Frankfurter Allgemeine Zeitung - 16 Oct 2018 Leben mit Rett-Syndrom: Plötzlich kamen keine Worte mehr ... More
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Documenting and sharing my daughter's life with Rett syndrome Rett Syndrome News - 25 Apr 2024 Documenting and sharing my daughter's life with Rett syndrome ... More
Mitochondrial modulation with leriglitazone as a potential treatment for Rett syndrome - Journal of Translational Medicine BioMed Central - 26 Oct 2023 Mitochondrial modulation with leriglitazone as a potential treatment for Rett syndrome - Journal of Translational Medicine ... More
Acadia Pharmaceuticals Announces Trofinetide New Drug Submission for Treatment of Rett Syndrome Has Been ... Business Wire - 22 Apr 2024 Acadia Pharmaceuticals Announces Trofinetide New Drug Submission for Treatment of Rett Syndrome Has Been ... ... More
Trofinetide for the treatment of Rett syndrome: a randomized phase 3 study Nature - 08 Jun 2023 Trofinetide for the treatment of Rett syndrome: a randomized phase 3 study ... More
Transformation of Rett Syndrome Research With the Emergence of Adult Data: Walter E. Kaufmann, MD Neurology live - 02 Feb 2024 Transformation of Rett Syndrome Research With the Emergence of Adult Data: Walter E. Kaufmann, MD ... More
Advances in Rett syndrome treatment: the rise of gene therapy Labiotech.eu - 14 Mar 2024 Advances in Rett syndrome treatment: the rise of gene therapy ... More
Neurogene doses two paediatric patients in trial of Rett Syndrome therapy Clinical Trials Arena - 01 Dec 2023 Neurogene doses two paediatric patients in trial of Rett Syndrome therapy ... More
Neurogene expands gene therapy clinical trial for Rett syndrome treatment biopharma-reporter.com - 05 Mar 2024 Neurogene expands gene therapy clinical trial for Rett syndrome treatment ... More
Neurogene Announces Upcoming Presentation of Safety Data from Phase 1/2 Trial of NGN-401 Gene Therapy for Rett ... Business Wire - 22 Apr 2024 Neurogene Announces Upcoming Presentation of Safety Data from Phase 1/2 Trial of NGN-401 Gene Therapy for Rett ... ... More
Abnormal spectral and scale-free properties of resting-state EEG in girls with Rett syndrome | Scientific Reports Nature - 09 Aug 2023 Abnormal spectral and scale-free properties of resting-state EEG in girls with Rett syndrome | Scientific Reports ... More
Neurogene expanding, updating NGN-401 Rett gene therapy trial Rett Syndrome News - 13 Mar 2024 Neurogene expanding, updating NGN-401 Rett gene therapy trial ... More
VIBRANT study to test ways to monitor symptoms of Rett syndrome Rett Syndrome News - 03 Apr 2024 VIBRANT study to test ways to monitor symptoms of Rett syndrome ... More